著者名,論文名,雑誌名,ISSN,出版者名,出版日付,巻,号,ページ,URL,URL(DOI) Sandra Motas and Virginia Haurigot and Miguel Garcia and Sara Marcó and Albert Ribera and Carles Roca and Xavier Sánchez and Víctor Sánchez and Maria Molas and Joan Bertolin and Luca Maggioni and Xavier León and Jesús Ruberte and Fatima Bosch,CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome),JCI Insight,2379-3708,American Society for Clinical Investigation,2016-06-16,1,9,e86696,https://cir.nii.ac.jp/crid/1360011143673509504,https://doi.org/10.1172/jci.insight.86696