著者名,論文名,雑誌名,ISSN,出版者名,出版日付,巻,号,ページ,URL,URL(DOI) Florian Eichler and Christine Duncan and Patricia L. Musolino and Paul J. Orchard and Satiro De Oliveira and Adrian J. Thrasher and Myriam Armant and Colleen Dansereau and Troy C. Lund and Weston P. Miller and Gerald V. Raymond and Raman Sankar and Ami J. Shah and Caroline Sevin and H. Bobby Gaspar and Paul Gissen and Hernan Amartino and Drago Bratkovic and Nicholas J.C. Smith and Asif M. Paker and Esther Shamir and Tara O’Meara and David Davidson and Patrick Aubourg and David A. Williams,Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy,New England Journal of Medicine,0028-4793,Massachusetts Medical Society,2017-10-26,377,17,1630-1638,https://cir.nii.ac.jp/crid/1360292621169389056,https://doi.org/10.1056/nejmoa1700554