著者名,論文名,雑誌名,ISSN,出版者名,出版日付,巻,号,ページ,URL,URL(DOI) Cristin D Davidson and Alana L Gibson and Tansy Gu and Laura L Baxter and Benjamin E Deverman and Keith Beadle and Arturo A Incao and Jorge L Rodriguez-Gil and Hideji Fujiwara and Xuntian Jiang and Randy J Chandler and Daniel S Ory and Viviana Gradinaru and Charles P Venditti and William J Pavan,Improved systemic AAV gene therapy with a neurotrophic capsid in Niemann–Pick disease type C1 mice,Life Science Alliance,2575-1077,"Life Science Alliance, LLC",2021-08-18,4,10,e202101040,https://cir.nii.ac.jp/crid/1360294812152666496,https://doi.org/10.26508/lsa.202101040