著者名,論文名,雑誌名,ISSN,出版者名,出版日付,巻,号,ページ,URL,URL(DOI) Lindsey A. George and Spencer K. Sullivan and Adam Giermasz and John E.J. Rasko and Benjamin J. Samelson-Jones and Jonathan Ducore and Adam Cuker and Lisa M. Sullivan and Suvankar Majumdar and Jerome Teitel and Catherine E. McGuinn and Margaret V. Ragni and Alvin Y. Luk and Daniel Hui and J. Fraser Wright and Yifeng Chen and Yun Liu and Katie Wachtel and Angela Winters and Stefan Tiefenbacher and Valder R. Arruda and Johannes C.M. van der Loo and Olga Zelenaia and Daniel Takefman and Marcus E. Carr and Linda B. Couto and Xavier M. Anguela and Katherine A. High,Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant,New England Journal of Medicine,0028-4793,Massachusetts Medical Society,2017-12-07,377,23,2215-2227,https://cir.nii.ac.jp/crid/1362262943501860224,https://doi.org/10.1056/nejmoa1708538