Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy
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- Jerry R. Mendell
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Zarife Sahenk
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Kelly Lehman
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Carrie Nease
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Linda P. Lowes
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Natalie F. Miller
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Megan A. Iammarino
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Lindsay N. Alfano
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Amanda Nicholl
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Samiah Al-Zaidy
- Department of Pediatrics, The Ohio State University, Columbus
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- Sarah Lewis
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Kathleen Church
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Richard Shell
- Department of Pediatrics, The Ohio State University, Columbus
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- Linda H. Cripe
- Department of Pediatrics, The Ohio State University, Columbus
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- Rachael A. Potter
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Danielle A. Griffin
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Eric Pozsgai
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
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- Ashish Dugar
- Sarepta Therapeutics Inc, Cambridge, Massachusetts
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- Mark Hogan
- Department of Radiology, Vascular and Interventional Radiology, Nationwide Children's Hospital, Columbus, Ohio
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- Louise R. Rodino-Klapac
- Center for Gene Therapy, The Abigail Wexner Research Institute at Nationwide Children’s Hospital, Columbus, Ohio
書誌事項
- タイトル別名
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- A Nonrandomized Controlled Trial
収録刊行物
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- JAMA Neurology
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JAMA Neurology 77 (9), 1122-, 2020-09-01
American Medical Association (AMA)