Targeting the Root Cause of Mucopolysaccharidosis IIIA with a New scAAV9 Gene Replacement Vector
Journal
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- Molecular Therapy - Methods & Clinical Development
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Molecular Therapy - Methods & Clinical Development 19 474-485, 2020-12
Elsevier BV
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Details 詳細情報について
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- CRID
- 1360580238114650496
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- ISSN
- 23290501
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- Data Source
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- Crossref