A Pilot Study of <i>In Vivo</i> Liver-Directed Gene Transfer with an Adenoviral Vector in Partial Ornithine Transcarbamylase Deficiency
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- Steven E. Raper
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Surgery, University of Pennsylvania, Philadelphia, PA 19104
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- Marc Yudkoff
- Department of Pediatrics, University of Pennsylvania, Philadelphia, PA 19104 and Children's Hospital of Philadelphia, Philadelphia, PA 19104
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- Narendra Chirmule
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104
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- Guang-Ping Gao
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104
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- Fred Nunes
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Medicine, University of Pennsylvania, Philadelphia, PA 19104
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- Ziv J. Haskal
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Radiology, University of Pennsylvania, Philadelphia, PA 19104
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- Emma E. Furth
- Department of Pathology and Laboratory Medicine, University of Pennsylvania, Philadelphia, PA 19104
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- Kathleen J. Propert
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Biostatistics and Epidemiology, University of Pennsylvania, Philadelphia, PA 19104
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- Michael B. Robinson
- Department of Pediatrics, University of Pennsylvania, Philadelphia, PA 19104 and Children's Hospital of Philadelphia, Philadelphia, PA 19104
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- Susan Magosin
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104
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- Heather Simoes
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104
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- Lisa Speicher
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104
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- Joseph Hughes
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104
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- John Tazelaar
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104
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- Nelson A. Wivel
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104 and Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104
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- James M. Wilson
- Institute for Human Gene Therapy, University of Pennsylvania, Philadelphia, PA 19104; Department of Molecular and Cellular Engineering, University of Pennsylvania, Philadelphia, PA 19104 and Department of Medicine, University of Pennsylvania, Philadelphia, PA 19104
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- Mark L. Batshaw
- Department of Pediatrics, University of Pennsylvania, Philadelphia, PA 19104; Children's Hospital of Philadelphia, Philadelphia, PA 19104 and George Washington University School of Medicine and Health Sciences and Children's National Medical Center, Washington, DC 20008
書誌事項
- 公開日
- 2002-01
- 権利情報
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- http://www.liebertpub.com/nv/resources-tools/text-and-data-mining-policy/121/
- DOI
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- 10.1089/10430340152712719
- 公開者
- SAGE Publications
この論文をさがす
収録刊行物
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- Human Gene Therapy
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Human Gene Therapy 13 (1), 163-175, 2002-01
SAGE Publications