Tafamidis for transthyretin familial amyloid polyneuropathy

  • Teresa Coelho
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Luis F. Maia
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Ana Martins da Silva
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Marcia Waddington Cruz
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Violaine Planté-Bordeneuve
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Pierre Lozeron
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Ole B. Suhr
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Josep M. Campistol
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Isabel Maria Conceição
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Hartmut H.-J. Schmidt
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Pedro Trigo
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Jeffery W. Kelly
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Richard Labaudinière
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Jason Chan
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Jeff Packman
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Amy Wilson
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Donna R. Grogan
    From the Hospital de Santo António (T.C., A.M.d.S.), Porto, Portugal; Department of Cellular Neurology (L.M.), Hertie Institute for Clinical Brain Research, Tübingen, Germany; Hospital Universitário Clementino Fraga Filho–UFRJ (M.W.C.), Rio de Janeiro, Brazil; CHU Henri Mondor (V.P.-B.), Créteil; CHU de Bicêtre (P.L.), Bicêtre, France; Department of Public Health and Clinical Medicine (O.B.S.), Umeå University, Umeå, Sweden; Hospital Clínic de Barcelona (J.M.C.), Barcelona, Spain; Hospital de Santa...
  • Oscar C Imventarza
    Fundaciónpara la Lucha contra las Enfermedades Neurológicas de la Infancia, Sub Investigator
  • Pablo J Wainberg
    Fundaciónpara la Lucha contra las Enfermedades Neurológicas de la Infancia, Sub Investigator
  • Lucas M Berra
    Fundaciónpara la Lucha contra las Enfermedades Neurológicas de la Infancia, Sub Investigator
  • Henryk Maultasch
    Hospital Universitário Clementino Fraga Filho-UFRJ, Sub Investigator
  • Jaime Gold
    Hospital Universitário Clementino Fraga Filho-UFRJ, Sub Investigator
  • Juan Carlos Pare Bardera
    Hospital Clínic de Barcelona, Sub Investigator
  • Andree Zibert
    Universitatsklinikum Münster, Sub Investigator

書誌事項

タイトル別名
  • A randomized, controlled trial

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収録刊行物

  • Neurology

    Neurology 79 (8), 785-792, 2012-08-21

    Ovid Technologies (Wolters Kluwer Health)

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