Delivery and Specificity of CRISPR/Cas9 Genome Editing Technologies for Human Gene Therapy
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- Jennifer L. Gori
- Editas Medicine, Cambridge, Massachusetts.
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- Patrick D. Hsu
- Editas Medicine, Cambridge, Massachusetts.
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- Morgan L. Maeder
- Editas Medicine, Cambridge, Massachusetts.
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- Shen Shen
- Editas Medicine, Cambridge, Massachusetts.
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- G. Grant Welstead
- Editas Medicine, Cambridge, Massachusetts.
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- David Bumcrot
- Editas Medicine, Cambridge, Massachusetts.
収録刊行物
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- Human Gene Therapy
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Human Gene Therapy 26 (7), 443-451, 2015-07
Mary Ann Liebert Inc