Pediatric acute myeloid leukemia with t(8;16)(p11;p13), a distinct clinical and biological entity: a collaborative study by the International-Berlin-Frankfurt-Münster AML-study group

  • Eva A. Coenen
    Department of Pediatric Oncology/Hematology, Erasmus MC-Sophia Children’s Hospital, Rotterdam, The Netherlands;
  • C. Michel Zwaan
    Department of Pediatric Oncology/Hematology, Erasmus MC-Sophia Children’s Hospital, Rotterdam, The Netherlands;
  • Dirk Reinhardt
    Acute Myeloid Leukemia-Berlin-Frankfurt-Münster Study Group, Pediatric Hematology/Oncology, Medical School Hannover, Hannover, Germany;
  • Christine J. Harrison
    Northern Institute of Cancer Research, Newcastle University, Newcastle upon Tyne, United Kingdom;
  • Oskar A. Haas
    St. Anna Children's Hospital and Children’s Cancer Research Institute, Department of Pediatrics, Medical University of Vienna, Vienna, Austria;
  • Valerie de Haas
    Dutch Childhood Oncology Group, the Hague, The Netherlands;
  • Vladimir Mihál
    Czech Pediatric Hematology/Oncology, Department of Pediatrics, University Hospital, Palacky´s University, Olomouc, Czech Republic;
  • Barbara De Moerloose
    Belgian Society of Paediatric Haematology Oncology, Ghent University Hospital, Department of Pediatric Hematology/Oncology, Ghent, Belgium;
  • Marta Jeison
    Cancer Cytogenetic Laboratory, Pediatric Hematology Oncology Department, Schneider Children's Medical Center of Israel, Petach Tikvah, Israel;
  • Jeffrey E. Rubnitz
    St. Jude Children’s Research Hospital, Memphis, TN;
  • Daisuke Tomizawa
    Japanese Pediatric Leukemia/Lymphoma Study Group, Department of Pediatrics, Tokyo Medical and Dental University, Tokyo, Japan;
  • Donna Johnston
    Children’s Oncology Group, Arcadia, CA;
  • Todd A. Alonzo
    Children’s Oncology Group, Arcadia, CA;
  • Henrik Hasle
    Nordic Society for Pediatric Hematology and Oncology, Department of Pediatrics, Aarhus University Hospital Skejby, Aarhus, Denmark;
  • Anne Auvrignon
    French Leucémie Aique Myeloide Enfant, Hopital Trousseau, Paris, France;
  • Michael Dworzak
    St. Anna Children's Hospital and Children’s Cancer Research Institute, Department of Pediatrics, Medical University of Vienna, Vienna, Austria;
  • Andrea Pession
    Italian Association of Pediatric Hematology Oncology, Clinica Pediatrica, Università Padova, Padova, Italy;
  • Vincent H. J. van der Velden
    Department of Immunology, Erasmus MC, Rotterdam, The Netherlands;
  • John Swansbury
    Department of Clinical Cytogenetics, The Royal Marsden Hospital and The Institute of Cancer Research, Sutton, United Kingdom;
  • Kit-fai Wong
    Department of Pathology, Queen Elizabeth Hospital, Hong Kong, China;
  • Kiminori Terui
    Department of Pediatrics, Hirosaki University Graduate School of Medicine, Hirosaki, Japan;
  • Sureyya Savasan
    Division of Hematology/Oncology, Children’s Hospital of Michigan, Detroit, MI;
  • Mark Winstanley
    Department of Pediatric Oncology, Starship Children’s Hospital, Auckland, New Zealand; and
  • Goda Vaitkeviciene
    Clinic for Children’s Diseases, Centre for Oncology/Haematology, Vilnius University, Vilnius, Lithuania
  • Martin Zimmermann
    Acute Myeloid Leukemia-Berlin-Frankfurt-Münster Study Group, Pediatric Hematology/Oncology, Medical School Hannover, Hannover, Germany;
  • Rob Pieters
    Department of Pediatric Oncology/Hematology, Erasmus MC-Sophia Children’s Hospital, Rotterdam, The Netherlands;
  • Marry M. van den Heuvel-Eibrink
    Department of Pediatric Oncology/Hematology, Erasmus MC-Sophia Children’s Hospital, Rotterdam, The Netherlands;

抄録

<jats:title>Key Points</jats:title><jats:p>Pediatric t(8;16)(p11;p13) AML is a rare entity defined by a unique gene expression signature and distinct clinical features. Spontaneous remissions occur in a subset of neonatal t(8;16)(p11;p13) AML cases.</jats:p>

収録刊行物

  • Blood

    Blood 122 (15), 2704-2713, 2013-10-10

    American Society of Hematology

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